For a Rare Disease Drug Trials Scramble for Patients

Aug 20, 2015, 09:05 by Michael Croft

WSJ | After years of effort, scientists and families of young patients with a rare genetic condition are facing the prospect of three companies launching clinical trials to develop therapies. But can the community support more than one trial at the same time?

August 20, 2015 | After years of effort, scientists and families of young patients with a rare genetic condition are facing the prospect of three companies launching clinical trials to develop therapies. But can the community support more than one trial at the same time? WSJ